{"id":4195,"date":"2020-04-28T11:41:00","date_gmt":"2020-04-28T09:41:00","guid":{"rendered":"https:\/\/patientenstimme-sma.de\/?page_id=4195"},"modified":"2026-03-16T21:04:50","modified_gmt":"2026-03-16T20:04:50","slug":"risdiplam-studie-firefish-part-2-erreicht-primaeren-endpunkt","status":"publish","type":"post","link":"https:\/\/smartunity.space\/stories\/thema\/risdiplam-studie-firefish-part-2-erreicht-primaeren-endpunkt\/","title":{"rendered":"Risdiplam Studie &#8220;FIREFISH &#8211; Part 2&#8221; erreicht prim\u00e4ren Endpunkt"},"content":{"rendered":"\n<p class=\"tw-text-wide\">Wie Roche heute in einer Pressemitteilung bekannt gab, erreichte Teil 2 der Firefish Studie ihren prim\u00e4ren Endpunkt. Dieser war, zu sehen, wie viele von insgesamt 41 eingeschlossen Typ1 S\u00e4uglingen im Alter von 1 &#8211; 7 Monaten, nach 12 monatiger Behandlung, gemessen an den <strong><a rel=\"noreferrer noopener\" href=\"https:\/\/de.wikipedia.org\/wiki\/Bayley_Scales_of_Infant_Development\" target=\"_blank\">Bayley Scales of Invant Development<\/a><\/strong>, mindestens 5 Sekunden frei und ohne Unterst\u00fctzung sitzen k\u00f6nnen. Im Ergebniss konnten dies 12\/41 erreichen. Desweiteren konnten 18  den Kopf aufrecht halten, 13 zur Seite rollen und 2 nach Klassifizierung des Hammersmith Infant Neurology mit Unterst\u00fctzung stehen.<\/p>\n\n\n\n<p class=\"tw-text-wide\">Quelle: <a rel=\"noreferrer noopener\" href=\"https:\/\/www.roche.com\/media\/releases\/med-cor-2020-04-28.htm\" target=\"_blank\">Roche Mediarelease<\/a><\/p>\n","protected":false},"excerpt":{"rendered":"<p>Wie Roche heute in einer Pressemitteilung bekannt gab, erreichte Teil 2 der Firefish Studie ihren prim\u00e4ren Endpunkt. Dieser war, zu sehen, wie viele von insgesamt 41 eingeschlossen Typ1 S\u00e4uglingen im Alter von 1 &#8211; 7 Monaten, nach 12 monatiger Behandlung, gemessen an den Bayley Scales of Invant Development, mindestens 5 Sekunden frei und ohne Unterst\u00fctzung [&hellip;]<\/p>\n","protected":false},"author":1,"featured_media":0,"comment_status":"closed","ping_status":"closed","sticky":false,"template":"only-view","format":"standard","meta":{"activitypub_content_warning":"","activitypub_content_visibility":"","activitypub_max_image_attachments":0,"activitypub_interaction_policy_quote":"anyone","activitypub_status":"","footnotes":""},"categories":[1],"tags":[58],"class_list":["post-4195","post","type-post","status-publish","format-standard","hentry","category-thema","tag-smanews"],"_links":{"self":[{"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/posts\/4195","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/comments?post=4195"}],"version-history":[{"count":1,"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/posts\/4195\/revisions"}],"predecessor-version":[{"id":39831,"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/posts\/4195\/revisions\/39831"}],"wp:attachment":[{"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/media?parent=4195"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/categories?post=4195"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/smartunity.space\/stories\/wp-json\/wp\/v2\/tags?post=4195"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}